|
Enzyme replacement therapy with alglucosidase alfa in Pompe disease: Clinical experience with rate escalation (2017)
|
30.11.-0001 |
|
Insights and Best Practices for Planning and Implementing Patient Advisory Boards (2017)
|
15.02.2018 |
|
Long-term benefit of enzyme replacement therapy in Pompe disease (2017)
|
30.11.-0001 |
|
Newborn Screening for Pompe Disease (2017)
|
04.01.2018 |
|
Pompe disease in Austria: clinical, genetic and epidemiological aspects (2017)
|
30.11.-0001 |
|
The humanistic burden of Pompe disease: are there still unmet needs? A systematic review. (2017)
|
30.11.-0001 |
